99503014
Nov 18, 2025
Pharmaceutical preparations and substances for the treatment of neurodevelopmental and neurodegenerative diseases and disorders, leukodystrophy, demyelinating diseases and disorders, and hypomyelinating diseases and disorders; Pharmaceutical preparations and substances for the treatment of glial fibrillary acidic protein-associated diseases and disorders, Alexander Disease, seizures, ataxia, motor function disorders, cognitive function disorders, dysphagia, and swallowing disorders; Pharmaceutical preparations and substances for the treatment of autosomal dominant, autosomal recessive, genetic, neurologic, parasympathetic system, neuromuscular system, skeletomuscular system, central nervous system, epileptic, pulmonary, respiratory, ophthalmic, gastrointestinal, skin, metabolic, autoimmune and lymphoproliferative diseases and disorders; Pharmaceutical preparations containing zilganersen.
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