VALSCIENT

Pharmaceutical preparations for diagnosis, prevention and treatment of diseases and disorders by gene therapy, namely, Parkinson's disease, Friedreich's ataxia and congenital birth defects; Pharmaceuticals for the treatment of rare and orphan diseases, disorders and conditions, namely, rare pediatric epilepsies, SCN8A developmental and epileptic encephalopathy, and congenital adrenal hyperplasia; pharmaceutical preparations for the treatment of neurological, central nervous system, psychiatric and movement diseases, disorders and conditions; pharmaceutical preparations for the treatment of endocrine diseases, disorders and conditions; pharmaceutical preparations for the treatment of hormonal diseases, disorders and conditions; pharmaceutical preparations for the treatment of genetic diseases, disorders and conditions