SANGRAIL BIOLOGICS

Pharmaceutical preparations for treatment of rare genetic diseases; pharmaceutical preparations primarily comprising cells for treatment of rare diseases; pharmaceutical preparations and therapeutic agents for use in gene therapy; pharmaceutical preparations for gene therapy for the treatment of genetic diseases or disorders; pharmaceutical preparations for use in the treatment of gene therapy treatable diseases.

Medical and scientific research in the field of gene therapy; medical and scientific research in the field of gene editing for developing cells and pharmaceuticals for medical and clinical use. Research and development of pharmaceuticals using gene editing