REGENXBIO

Custom development of biochemical reagents, namely, synthesis for others of clinical medical reagents for use in gene therapy, development of pharmaceutical preparations for use in gene therapy, and therapeutic compositions that include recombinant adeno-associated viral (rAAV) vectors to provide a platform for specific expression of biologics with therapeutic effect in gene therapy, and RNA interference (RNAi); Scientific and medical research and development; genetic engineering services, biotechnology research services, and research and development of new products in the field of gene therapeutics and research tools, including those based on recombinant adeno-associated viral vectors