NAV

Clinical medical reagents for use in gene therapy; pharmaceutical preparations for use in gene therapy; therapeutic pharmaceutical compositions that include recombinant adenoassociated viral (rAAV) vectors to provide a platform for specific expression of biologics with therapeutic effect in gene therapy, RNA interference (RNAi), and cell therapy; pharmaceutical preparations containing adeno-associated virus (AAV) vectors and nucleic acid for a system delivering genes to biological cells for use in the treatment of diseases, sicknesses, and disorders, namely, neurodegenerative disorders, metabolic and hematologic disorders, cardiovascular, oncologic and ocular diseases