LENMELDY

Pharmaceutical preparations for the treatment of orphan diseases, namely, inherited disorders of the immune system, inherited metabolic disorders, inherited blood disorders, inherited neuro-degenerative disorders; Chemical preparations for pharmaceutical or medical purposes for use in gene therapy for the treatment of orphan diseases, namely, inherited disorders of the immune system, inherited metabolic disorders, inherited blood disorders, inherited neuro-degenerative disorders; Medicinal preparations for the treatment of orphan diseases, namely, inherited disorders of the immune system, inherited metabolic disorders, inherited blood disorders, inherited neuro-degenerative disorders