CTX450

Cells for medical or clinical use in the field of in vivo gene editing therapy for the treatment of liver, neurological, and neurovascular diseases or conditions; pharmaceutical and biopharmaceutical agents for the treatment of liver, neurological, and neurovascular diseases or conditions in the field of in vivo gene editing therapy; gene therapy products, namely, gene transfer, regulation, modulation and delivery pharmaceuticals for the treatment of liver, neurological, and neurovascular diseases or conditions in the field of in vivo gene editing therapy

Gene editing, namely, medical and scientific research for the treatment of genetic diseases and disorders in the field of in vivo gene editing therapy; gene editing, namely, pharmaceutical research and development in the field of in vivo gene editing therapy